Empowering access to orphan drugs and non-commercially viable medicines

Orphan drugs are medicines developed to treat rare diseases. They often receive little attention from major pharmaceutical companies due to their limited market demand and low profitability. In Malaysia, many of these drugs have to be imported or require special approval, resulting in inconsistent supply and issues with accessibility for patients. Yet, despite their small market, orphan medicines play a vital role in advancing medical innovation and safeguarding public health.